BAKER BROS. ADVISORS LP Q2 2017 Filing

Filed August 14, 2017

Portfolio Value

$11.4B

Holdings

120

Report Date

Q2 2017

Filing Type

13F-HR

All Holdings (120 positions)

#StockSharesValue% PortfolioType
1
INCYIncyte Corporation
34,130,161$4.3T37569.23%
2
SGENEURSeattle Genetics, Inc.
45,725,556$2.4T20683.27%
3
ALXNAlexion Pharmaceuticals, Inc.
8,553,864$1.0T9098.71%
4
ACADACADIA Pharmaceuticals Inc.
25,819,768$720.1B6295.56%
5
BMRNBioMarin Pharmaceutical Inc.
5,905,673$536.4B4689.05%
6
Genomic Health, Inc.
13,779,866$448.5B3921.30%
7
DBV Technologies S.A.
5,509,560$196.7B1720.04%
8
ONCBeiGene, Ltd.
3,673,175$165.3B1445.07%
9
Aquinox Pharmaceuticals, Inc.
10,934,154$153.8B1344.98%
10
Achaogen, Inc.
4,804,604$104.4B912.75%
11
AMRNAmarin Corporation plc
22,669,509$91.4B798.69%
12
Advanced Accelerator Applications S.A.
2,221,706$86.7B758.28%
13
Spark Therapeutics, Inc.
1,318,341$78.8B688.54%
14
NVTA1EURInvitae Corporation
7,288,300$69.7B609.14%
15
BCRXBioCryst Pharmaceuticals, Inc.
11,716,784$65.1B569.53%
16
Bellicum Pharmaceuticals, Inc.
5,032,313$58.8B513.86%
17
AveXis, Inc.
625,000$51.4B448.93%
18
EX9Exelixis, Inc.
2,082,012$51.3B448.31%
19
ASNDAscendis Pharma A/S
1,751,463$48.6B425.07%
20
NVAX 3.75 02/01/23Novavax, Inc.
108,500,000$46.4B405.90%
21
HRTXHeron Therapeutics, Inc.
2,783,569$38.6B337.04%
22
GBYSangamo Therapeutics, Inc.
4,113,376$36.2B316.46%
23
bluebird bio, Inc.
301,441$31.7B276.84%
24
Acorda Therapeutics, Inc.
35,083,000$30.0B262.14%
25
Versartis, Inc.
1,660,593$29.0B253.33%
26
NBIXNeurocrine Biosciences, Inc.
616,682$28.4B248.00%
27
CERSCerus Corporation
10,241,943$25.7B224.74%
28
IMGNEURImmunoGen, Inc.
3,015,353$21.4B187.43%
29
Progenics Pharmaceuticals, Inc.
3,150,808$21.4B187.04%
30
HALOHalozyme Therapeutics, Inc.
1,581,424$20.3B177.24%
31
GLPGGalapagos NV
259,894$19.9B173.86%
32
XNCRXencor, Inc.
872,072$18.4B160.94%
33
MRUSMerus N.V.
1,160,014$18.4B160.74%
34
Idera Pharmaceuticals, Inc.
10,294,970$17.7B154.80%
35
NeuroDerm Ltd.
571,667$17.1B149.43%
36
NTLAIntellia Therapeutics, Inc.
1,062,120$17.0B148.57%
37
SG7Sage Therapeutics, Inc.
208,328$16.6B145.05%
38
AERIEURAerie Pharmaceuticals, Inc.
299,356$15.7B137.53%
39
La Jolla Pharmaceutical Company
504,732$15.0B131.36%
40
CPRXCatalyst Pharmaceuticals, Inc.
5,102,153$14.1B123.11%
41
Aimmune Therapeutics, Inc.
673,908$13.9B121.14%
42
BioMarin Pharmaceutical Inc.
12,228,000$13.5B118.43%
43
ARRYEURArray BioPharma Inc.
1,585,913$13.3B116.05%
44
Aegerion Pharmaceuticals, Inc.
14,517,000$11.5B100.97%
45
Foamix Pharmaceuticals Ltd.
2,466,702$11.4B100.06%
46
Loxo Oncology, Inc.
138,312$11.1B96.96%
47
Abeona Therapeutics Inc.
1,684,364$10.8B94.24%
48
Ignyta, Inc.
896,000$9.3B81.08%
49
Syros Pharmaceuticals, Inc.
574,835$9.2B80.86%
50
LGNDLigand Pharmaceuticals Incorporated
73,386$8.9B77.89%
51
ALKSAlkermes plc
150,251$8.7B76.15%
52
Achillion Pharmaceuticals, Inc.
1,856,637$8.5B74.50%
53
MRTXEURMirati Therapeutics, Inc.
2,269,198$8.3B72.41%
54
ITCIEURIntra-Cellular Therapies, Inc.
609,166$7.6B66.15%
55
CBAYUSDCymaBay Therapeutics, Inc.
1,291,775$7.4B65.05%
56
RIGLUSDRigel Pharmaceuticals, Inc.
2,518,882$6.9B60.12%
57
IM8NInsmed Incorporated
400,000$6.9B60.01%
58
AGIOAgios Pharmaceuticals, Inc.
128,666$6.6B57.88%
59
MGNXMacroGenics, Inc.
363,676$6.4B55.67%
60
GLYCEURGlycoMimetics, Inc.
563,312$6.3B54.96%
61
ContraFect Corporation
4,045,876$5.9B51.29%
62
Stemline Therapeutics, Inc.
633,497$5.8B50.95%
63
SELBUSDSelecta Biosciences, Inc.
289,809$5.8B50.32%
64
ASMBAssembly Biosciences, Inc.
250,000$5.2B45.14%
65
Spring Bank Pharmaceuticals, Inc.
373,144$5.1B44.17%
66
AGLEUSDAeglea BioTherapeutics, Inc.
1,137,872$4.4B38.30%
67
BDQMAlbireo Pharma, Inc.
200,000$4.1B36.02%
68
Array BioPharma Inc.
3,000,000$4.1B35.55%
69
NewLink Genetics Corporation
500,000$3.7B32.13%
70
Nabriva Therapeutics plc
350,000$3.7B32.07%
71
Epizyme, Inc.
232,481$3.5B30.69%
72
OVIDOvid Therapeutics Inc.
333,333$3.5B30.57%
73
Ra Pharmaceuticals, Inc.
177,952$3.3B29.16%
74
Adamas Pharmaceuticals, Inc.
172,630$3.0B26.39%
75
Inotek Pharmaceuticals Corporation
5,000,000$3.0B26.04%
76
ANABAnaptysBio, Inc.
117,211$2.8B24.52%
77
Zogenix, Inc.
185,290$2.7B23.49%
78
Protalix BioTherapeutics, Inc.
3,423,000$2.6B22.49%
79
Alder BioPharmaceuticals, Inc.
217,328$2.5B21.75%
80
NTRANatera, Inc.
228,676$2.5B21.71%
81
NVAXNovavax, Inc.
2,000,000$2.3B20.11%
82
Akari Therapeutics plc
496,901$2.3B20.03%
83
Tonix Pharmaceuticals Holding Corp.
510,922$2.2B19.34%
84
Trevena, Inc.
950,000$2.2B19.10%
85
Aevi Genomic Medicine, Inc.
1,618,089$2.2B18.81%
86
ARGXargenx SE
100,000$2.1B18.54%
87
Sunesis Pharmaceuticals, Inc.
741,665$2.0B17.50%
88
KPTIEURKaryopharm Therapeutics Inc.
216,990$2.0B17.17%
89
TREURTrillium Therapeutics Inc.
413,697$1.8B15.91%
90
Dimension Therapeutics, Inc.
1,251,881$1.8B15.87%
91
RAREUltragenyx Pharmaceutical Inc.
25,000$1.6B13.58%
92
MediWound Ltd.
226,000$1.5B13.44%
93
Juno Therapeutics, Inc.
50,000$1.5B13.07%
94
Immune Design Corp.
148,937$1.5B12.69%
95
MCRB1EURSeres Therapeutics, Inc.
125,000$1.4B12.35%
96
JNCEEURJounce Therapeutics, Inc.
100,000$1.4B12.27%
97
MyoKardia, Inc.
100,000$1.3B11.45%
98
CLLSCellectis S.A.
50,000$1.3B11.29%
99
InVivo Therapeutics Holdings Corp.
400,000$1.1B9.44%
100
MDGLMadrigal Pharmaceuticals, Inc.
57,762$939.0M8.21%
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